Overview

Definition:
-Idiopathic Thrombocytopenic Purpura (ITP) is an autoimmune disorder characterized by isolated thrombocytopenia (low platelet count) in the absence of any other identifiable cause, leading to increased bleeding risk
-In children, it is often acute and self-limiting, typically occurring after a viral infection.
Epidemiology:
-ITP is the most common acquired bleeding disorder in childhood, with an incidence of approximately 3-8 per 100,000 children per year
-It can occur at any age, but peaks are seen between 2-6 years and in adolescence
-There is no significant sex predilection in younger children, but adolescent girls may be more commonly affected.
Clinical Significance:
-Understanding activity restrictions and bleeding precautions is crucial for preventing serious hemorrhagic complications in children with ITP
-These measures are vital for guiding parents and caregivers, ensuring safe participation in school and daily activities, and minimizing the risk of trauma-induced bleeding
-For DNB and NEET SS preparation, this topic frequently appears in clinical scenarios requiring practical management advice.

Clinical Presentation

Symptoms:
-Easy bruising (ecchymoses)
-Petechiae, often on lower extremities
-Nosebleeds (epistaxis) that are difficult to control
-Bleeding gums
-Blood in urine (hematuria) or stool (melena)
-Heavy menstrual bleeding in adolescent females
-In severe cases, intracranial hemorrhage (rare).
Signs:
-Isolated thrombocytopenia (<100 x 10^9/L) on peripheral blood smear
-Normal or slightly enlarged spleen
-Absence of fever, lymphadenopathy, or hepatosplenomegaly suggesting other causes of thrombocytopenia
-Petechiae and purpura visible on skin and mucous membranes
-Vital signs may be normal unless significant blood loss is present.
Diagnostic Criteria:
-Diagnosis is primarily based on clinical presentation and laboratory findings
-Criteria include: isolated thrombocytopenia (<100 x 10^9/L) with normal white blood cell and red blood cell counts
-absence of fever, lymphadenopathy, hepatosplenomegaly, or congenital anomalies
-normal coagulation profile (PT, aPTT)
-and absence of another identifiable cause of thrombocytopenia (e.g., infections, toxins, other autoimmune diseases)
-Presence of antiplatelet antibodies can support the diagnosis but is not routinely required.

Management Activity Restrictions

Platelet Count Thresholds:
-Activity restrictions are guided by the platelet count and bleeding severity
-Generally: Platelet count >50 x 10^9/L: No restrictions, normal activity allowed
-Platelet count 20-50 x 10^9/L: Avoid contact sports, high-risk activities, and unsupervised play
-Encourage less vigorous activities
-Platelet count <20 x 10^9/L: Strict avoidance of contact sports, rough play, and any activity with a risk of head injury or significant trauma
-Supervised activities only
-Platelet count <10 x 10^9/L: Consider hospitalization and stricter precautions
-Avoid all contact sports and activities with even minor risk of injury.
School And Extracurricular Activities:
-When platelet counts are acceptable, children can attend school and participate in most activities
-However, coaches, teachers, and parents must be informed
-Contact sports (e.g., football, rugby, martial arts) are generally contraindicated until platelet counts are consistently above 50 x 10^9/L
-Activities like swimming, cycling (with helmet), and team sports with less physical contact may be permissible with lower counts, depending on individual assessment.
Head Injury Prevention:
-This is paramount
-Children with ITP, especially those with platelet counts <20 x 10^9/L, must wear helmets for cycling, skateboarding, and other activities that pose a risk of head trauma
-Parents should be educated on recognizing signs of intracranial hemorrhage (severe headache, vomiting, altered mental status, focal neurological deficits) and seek immediate medical attention.
Travel And Environmental Considerations:
-Travel to remote areas or places with limited access to medical care may require careful planning, especially if the child has a lower platelet count
-Advise parents to carry relevant medical information and a supply of any prescribed medications
-Avoid activities that increase the risk of injury in potentially hazardous environments.

Management Bleeding Precautions

Home Safety Measures:
-Childproof the home to minimize accidental injuries
-Remove sharp objects, sharp corners on furniture, and tripping hazards
-Ensure adequate lighting
-Supervise young children closely
-Use soft bedding and appropriate safety gates.
Medication Avoidance:
-Strict avoidance of aspirin, NSAIDs (like ibuprofen), and other antiplatelet or anticoagulant medications is essential, as they can exacerbate bleeding
-Acetaminophen (paracetamol) is the preferred analgesic for pain management.
Oral Hygiene:
-Gentle oral hygiene practices are recommended
-Use a soft-bristled toothbrush and avoid vigorous brushing that can lead to gum bleeding
-If mouth sores or bleeding gums are significant, consult the hematologist.
Managing Minor Bleeding:
-For minor cuts and abrasions, apply direct pressure for 5-10 minutes
-For nosebleeds, have the child sit upright, lean forward, and pinch the soft part of the nose for 10-15 minutes
-If bleeding is prolonged or severe, seek medical advice
-Apply ice packs to bruises to help reduce swelling and pain.

Diagnostic Approach

History Taking:
-Key history points include the onset and duration of symptoms, presence and pattern of bleeding (nosebleeds, gum bleeding, bruising, hematuria, melena), recent infections (viral prodrome), immunization history, family history of bleeding disorders, and any medications taken
-Red flags include severe headache, vomiting, altered consciousness, focal neurological signs, abdominal pain, or significant blood loss.
Physical Examination:
-Focus on a thorough skin and mucous membrane examination for petechiae, purpura, and ecchymoses
-Assess for signs of active bleeding
-Palpate the abdomen for splenomegaly or hepatomegaly
-Perform a complete neurological exam, especially if there are concerns for intracranial bleeding
-Check vital signs, including heart rate and blood pressure, to assess for hypovolemia.
Investigations:
-Complete Blood Count (CBC) with differential: Essential to confirm isolated thrombocytopenia and rule out other cytopenias
-Platelet count is critical
-Peripheral Blood Smear: To assess platelet morphology and rule out pseudothrombocytopenia or other causes of microangiopathic hemolytic anemia
-Coagulation Profile (PT, aPTT, INR): To ensure normal coagulation and rule out disseminated intravascular coagulation (DIC)
-Bleeding Time: Historically used, but less common now due to variability
-platelet function analyzers can assess platelet aggregation
-Bone Marrow Aspiration (optional): Reserved for cases where diagnosis is uncertain, to rule out other bone marrow disorders, or in children not responding to standard therapy
-It typically shows normal or increased megakaryocytes.
Differential Diagnosis:
-Conditions to consider include viral-induced thrombocytopenia, drug-induced thrombocytopenia, immune thrombocytopenias secondary to other autoimmune diseases (e.g., SLE), thrombotic thrombocytopenic purpura (TTP), hemolytic uremic syndrome (HUS), leukemia, and aplastic anemia
-Distinguishing features include the presence of other cytopenias, fever, organomegaly, neurological symptoms (TTP/HUS), or a clear history of drug exposure.

Management Medical

Observation Vs Treatment:
-For children with mild ITP (platelet count >20-30 x 10^9/L) and no significant bleeding, observation may be appropriate, as spontaneous remission is common
-Treatment is indicated for platelet counts <20-30 x 10^9/L, severe bleeding, or impending risk of severe hemorrhage
-The goal is to rapidly increase platelet counts to a safe level.
Pharmacological Treatment:
-First-line therapy typically includes: Corticosteroids: Prednisolone 1-2 mg/kg/day orally for 2-4 weeks, followed by a tapering dose
-Intravenous Immunoglobulin (IVIG): 1 g/kg/day for 1-2 days or 0.8-1 g/kg as a single dose
-This provides a rapid, albeit transient, increase in platelet count, useful for severe bleeding or before procedures
-Platelet Transfusions: Reserved for life-threatening bleeding or active intracranial hemorrhage, as they are transient and may induce alloimmunization.
Second Line Therapies:
-If first-line therapies fail or for chronic ITP, second-line options include: Romiplostim or Eltrombopag (thrombopoietin receptor agonists) - used in refractory or chronic ITP in older children, carefully monitored
-Rituximab - an anti-CD20 monoclonal antibody
-Immunosuppressants like Azathioprine or Cyclosporine.
Splenectomy:
-Rarely considered in children with chronic, refractory ITP that has failed multiple medical treatments
-It is usually a last resort due to increased risk of infection.

Prognosis

Factors Affecting Prognosis:
-Most children (80-85%) achieve remission within weeks to months
-Chronic ITP (persisting beyond 12 months) is less common, occurring in about 15-20% of cases
-Factors associated with chronic ITP include older age at diagnosis, severe bleeding at presentation, and low initial platelet counts
-The risk of severe bleeding, particularly intracranial hemorrhage, is low but significant.
Outcomes:
-The vast majority of children with acute ITP recover fully with no long-term sequelae
-In chronic ITP, management focuses on maintaining a safe platelet count to prevent bleeding, and the quality of life can be affected
-Recurrence of ITP is possible but uncommon.
Follow Up:
-Children with acute ITP should have regular follow-up with their pediatrician or hematologist to monitor platelet counts and assess for resolution of bleeding
-For those with chronic ITP, long-term follow-up is necessary to manage the condition, monitor for treatment side effects, and assess for potential complications like infections.

Key Points

Exam Focus:
-DNB/NEET SS exam questions often focus on differentiating ITP from other causes of thrombocytopenia, immediate management of bleeding, appropriate activity restrictions based on platelet count, and the role of steroids vs
-IVIG
-Understanding the safe analgesic choice (paracetamol over NSAIDs) is also key.
Clinical Pearls:
-Always ask about recent viral illnesses
-Educate parents thoroughly on activity restrictions and when to seek urgent care
-Remember that platelet transfusions are generally reserved for life-threatening bleeding, not for raising platelet counts to facilitate procedures unless absolutely necessary and closely monitored.
Common Mistakes:
-Over-treating mild ITP without significant bleeding
-failing to adequately educate parents on precautions
-prescribing NSAIDs or aspirin for pain management
-missing red flags for intracranial hemorrhage
-or not considering bone marrow biopsy in atypical presentations.