Overview

Definition:
-Short stature is defined as a height more than 2 standard deviations below the mean for age and sex, or below the third percentile
-It represents a failure to achieve genetic potential height
-Accurate assessment involves evaluating growth velocity, genetic potential, and skeletal maturation.
Epidemiology:
-Affects approximately 3% of the pediatric population
-The etiology is diverse, ranging from benign variants (familial short stature, constitutional delay of growth and puberty) to pathological conditions (endocrine disorders, genetic syndromes, chronic illnesses, skeletal dysplasias).
Clinical Significance:
-Identifying the cause of short stature is crucial for timely intervention, preventing long-term physical and psychosocial morbidity, and optimizing adult height
-Early diagnosis and treatment can significantly improve outcomes for conditions like growth hormone deficiency and hypothyroidism.

Midparental Height

Calculation:
-Midparental height (MPH) estimates the target adult height based on parental heights
-For boys: (Father's height + Mother's height + 13 cm) / 2
-For girls: (Father's height + Mother's height - 13 cm) / 2
-A standard deviation range (e.g., ± 8.5 cm) around the MPH provides a predicted adult height range.
Interpretation:
-A child's height falling within ± 8.5 cm of the MPH is generally considered within normal genetic potential
-Significant deviation suggests potential growth disorders, nutritional deficiencies, or chronic illnesses impacting growth.
Limitations:
-MPH does not account for precocious puberty, delayed puberty, or chronic diseases that may affect final adult height
-It serves as a baseline for genetic potential, not a definitive predictor of final height alone.

Bone Age Assessment

Definition:
-Bone age (BA) represents the developmental or skeletal maturity of an individual, assessed by radiographic examination of the bones, typically the hand and wrist
-It reflects the epiphyseal fusion status, which is influenced by hormones and overall health.
Methodology:
-The most common method is the Greulich and Pyle (G&P) atlas, which compares the child's skeletal maturation to standard X-rays
-The Tanner-Whitehouse (TW2 or TW3) method is more detailed, scoring individual bone development
-Radiographs of the left hand and wrist are standard.
Interpretation:
-A bone age equal to chronological age (CA) suggests normal skeletal maturation
-BA significantly delayed relative to CA (e.g., >2 years) may indicate constitutional delay of growth and puberty, hypothyroidism, or GH deficiency
-BA significantly advanced relative to CA may suggest precocious puberty or overexposure to exogenous steroids.

Diagnostic Approach

History Taking:
-Detailed birth history (gestational age, birth weight, length)
-Growth history (serial height measurements, growth charts)
-Nutritional status
-History of chronic illnesses (GI, renal, cardiac, pulmonary)
-Pubertal development (age of onset of secondary sexual characteristics)
-Family history of growth problems or endocrine disorders
-Medications (steroids)
-Social and emotional factors.
Physical Examination:
-Accurate anthropometric measurements (height, weight, head circumference)
-Assess proportionality
-Examine for dysmorphic features
-Assess Tanner stage of puberty
-Palpate thyroid
-Check for signs of rickets or other skeletal abnormalities
-Assess for signs of chronic disease
-Fundoscopic examination.
Investigations:
-Baseline laboratory tests: Complete blood count, ESR, CRP, electrolytes, BUN, creatinine, calcium, phosphate, alkaline phosphatase, liver function tests, urinalysis
-Endocrine evaluation: Thyroid function tests (TSH, free T4), IGF-1, IGFBP-3
-Consider GH stimulation tests if indicated
-Karyotype if genetic syndrome suspected
-Skeletal survey if multiple bone lesions are suspected
-Imaging: Bone age radiograph of the hand and wrist is essential
-Other imaging may be needed based on suspected etiology (e.g., renal ultrasound, cardiac echo).
Differential Diagnosis:
-Constitutional delay of growth and puberty (CDGP)
-Familial short stature (FSS)
-Growth hormone deficiency (GHD)
-Hypothyroidism
-Cushing's syndrome
-Rickets
-Malnutrition
-Chronic diseases (e.g., inflammatory bowel disease, celiac disease, renal failure)
-Genetic syndromes (e.g., Turner syndrome, Noonan syndrome, Down syndrome)
-Skeletal dysplasias (e.g., achondroplasia)
-Intrauterine growth restriction (IUGR) with failure to catch up.

Management Principles

Addressing Underlying Cause:
-Treatment is directed at the specific etiology
-For hypothyroidism, thyroid hormone replacement
-For GH deficiency, recombinant human growth hormone (rhGH) therapy
-For nutritional deficiencies, nutritional support and supplementation
-For chronic illnesses, optimizing management of the primary condition.
Growth Hormone Therapy:
-Indicated for idiopathic short stature (ISS) and confirmed GH deficiency
-Dosage is typically 0.2-0.3 mg/kg/week divided into daily subcutaneous injections, adjusted based on IGF-1 levels and growth response
-Requires regular monitoring of height velocity and IGF-1 levels.
Constitutional Delay Of Growth And Puberty:
-Often requires no specific treatment
-reassurance and monitoring are key
-In selected cases, a trial of low-dose sex hormones can accelerate growth and induce puberty if psychosocial concerns exist.
Supportive Care:
-Psychosocial support is vital for children with short stature
-Nutritional counseling
-Regular follow-up to monitor growth and treatment efficacy
-Educational support to address any academic challenges.

Key Points

Exam Focus:
-Understand the calculation and interpretation of midparental height
-Know the methods and interpretation of bone age assessment (G&P, Tanner-Whitehouse)
-Recognize indications for GH therapy and common etiologies of short stature.
Clinical Pearls:
-Always plot serial height measurements on appropriate growth charts
-A falling growth curve is more concerning than a single low height measurement
-Differentiate between familial short stature and constitutional delay from pathological causes.
Common Mistakes:
-Over-reliance on MPH without considering bone age or growth velocity
-Initiating GH therapy without confirmed diagnosis of GH deficiency or significant short stature
-Failing to investigate for underlying chronic illnesses or endocrine disorders.